熊本大学大学院生命科学研究部 遺伝子機能応用学分野

Combinatorial screening for therapeutics in ATTRv amyloidosis identifies naphthoquinone analogues as TTR-selective amyloid disruptors

Sasaki R, Suico M.A, Chosa K, Teranishi Y, Sato T, Kagami A, Kotani S, Kato H, Hitora Y, Tsukamoto S, Yamashita T, Yokoyama T, Mizuguchi M, Kai H, Shuto T.
J Pharmacol Sci . 2023 Jan;151(1):54-62. doi: 10.1016/j.jphs.2022.11.004. Epub 2022 Nov 29.